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Mutant muscle-specific enhancers

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专利名称:Mutant muscle-specific enhancers发明人:JAMES S. CHAMBERLAIN,STEPHEN D.

HAUSCHKA

申请号:AU2294102申请日:20010713公开号:AU2294102A公开日:20020130

摘要:The present invention relates to nucleic acid compositions and expressionsystems comprising muscle-specific regulatory elements, and methods for expressingheterologous DNA sequences in cells. In particular, the present invention providesmutant muscle-specific enhancers, genetic cassettes, and vectors useful in gene therapy,diagnostic assays, and other gene expression systems.

申请人:THE REGENTS OF THE UNIVERSITY OF MICHIGAN

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